NHS to offer ‘life-changing’ gene therapy for blood disorder thalassaemia

NHS to offer ‘life-changing’ gene therapy for blood disorder thalassaemia

Treatment may be offered to hundreds with severe form of disease, most often found in people of Mediterranean, Asian and Middle Eastern heritage

People living with a rare genetic blood disorder in England will be offered a “life-changing” new treatment on the NHS, in what has been described as a historic moment.

Casgevy, which is a one-off gene therapy, has been approved for use on the NHS in England for people living with a severe form of thalassaemia.

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